KUNMING -- A group of Chinese scientists has uncovered the mystery behind how an ancient gene regulates the development of brain folds, shedding new light on the evolution of the human brain.
Eye researchers at the Swiss city of Basel are hopeful of a breakthrough in the treatment for blind people after initial positive indications that a new form of therapy works. Blind people learning to see ... .
LGMDR2 is caused by mutations in the DYSF gene, which prevent the body from producing functional dysferlin ...Gene therapy offers a promising way to address the underlying cause of the disease by restoring dysferlin.
Perceive Bio is advancing novel gene therapy treatments in ophthalmology and related verticals ... VOY-101 is an investigational recombinant adeno-associated virus gene therapy encoding a form of the protective variant of ComplementFactor H.